We are eternally grateful to our incredible Natalie’s Wish supporters, donors and cystinosis families who gathered together to celebrate the research progress we have collectively funded, the event was a record-breaking success raising more than $4 million for cystinosis research in one evening!
The Natalie’s Wish Celebration was the grand finale of the three-day Day of Hope family conference. Cystinosis families from all over the world joined together to celebrate CRF’s latest milestone to honor Stéphanie Cherqui, PhD of UC San Diego, for the recent FDA approval of her groundbreaking stem cell and gene therapy treatment clinical trial for cystinosis.
It is because of your generous support and participation that brings us one step closer to the cure!